Li et al., 2014 - Muscle dysfunction and structural defects of dystrophin-null sapje mutant zebrafish larvae are rescued by ataluren treatment. FASEB journal : official publication of the Federation of American Societies for Experimental Biology   34(Suppl2):116-122 Full text @ FASEB J.
Human Disease / Model Data (1 Record)
Human Disease Fish Environment Evidence Code
Duchenne muscular dystrophy dmdta222a/ta222a standard conditions