PUBLICATION

Glucocerebrosidase deficiency in zebrafish affects primary bone ossification through increased oxidative stress and reduced Wnt/β-catenin signaling

Authors
Zancan, I., Bellesso, S., Costa, R., Salvalaio, M., Stroppiano, M., Hammond, C., Argenton, F., Filocamo, M., Moro, E.
ID
ZDB-PUB-141019-3
Date
2015
Source
Human molecular genetics   24(5): 1280-94 (Journal)
Registered Authors
Argenton, Francesco, Bellesso, Stefania, Costa, Roberto, Hammond, Chrissy, Moro, Enrico, Salvalaio, Marika, Zancan, Ilaria
Keywords
none
Datasets
GEO:GSE54754
MeSH Terms
  • Animals
  • Apoptosis
  • Biomarkers/blood
  • Bone Resorption/genetics
  • Bone Resorption/metabolism
  • Bone and Bones/metabolism
  • Cell Differentiation
  • Cell Proliferation
  • Cloning, Molecular
  • Disease Models, Animal
  • Gaucher Disease/genetics*
  • Gaucher Disease/pathology
  • Gene Expression Profiling
  • Gene Expression Regulation
  • Genotyping Techniques
  • Glucosylceramidase/genetics
  • Humans
  • Osteoblasts/cytology
  • Osteoblasts/metabolism
  • Osteogenesis/genetics*
  • Oxidative Stress*
  • Reactive Oxygen Species/metabolism
  • Wnt Signaling Pathway*
  • Zebrafish/genetics*
  • Zebrafish/metabolism
  • beta Catenin/genetics
  • beta Catenin/metabolism
PubMed
25326392 Full text @ Hum. Mol. Genet.
Abstract
Loss of lysosomal glucocerebrosidase (GBA1) function is responsible for several organ defects, including skeletal abnormalities in type 1 Gaucher disease (GD). Enhanced bone resorption by infiltrating macrophages has been proposed to lead to major bone defects. However, while more recent evidences support the hypothesis that osteoblastic bone formation is impaired, a clear pathogenetic mechanism has not been depicted yet. Here, by combining different molecular approaches, we show that Gba1 loss of function in zebrafish is associated with defective canonical Wnt signaling, impaired osteoblast differentiation and reduced bone mineralization. We also provide evidence that increased reactive oxygen species (ROS) production precedes the Wnt signaling impairment, which can be reversed upon human GBA1 overexpression. Type 1 GD patient fibroblasts similarly exhibit reduced Wnt signaling activity, as a consequence of increased beta catenin degradation. Our results support a novel model in which a primary defect in canonical Wnt signaling antecedes bone defects in type 1 GD.
Genes / Markers
Figures
Show all Figures
Expression
Phenotype
Mutations / Transgenics
Human Disease / Model
Sequence Targeting Reagents
Fish
Antibodies
Orthology
Engineered Foreign Genes
Mapping