PUBLICATION

OCRL1 modulates cilia length in renal epithelial cells

Authors
Rbaibi, Y., Cui, S., Mo, D., Carattino, M., Rohatgi, R., Satlin, L.M., Szalinski, C.M., Swanhart, L.M., Fölsch, H., Hukriede, N.A., and Weisz, O.A.
ID
ZDB-PUB-120612-1
Date
2012
Source
Traffic (Copenhagen, Denmark)   13(9): 1295-1305 (Journal)
Registered Authors
Hukriede, Neil
Keywords
Lowe syndrome, phosphatidylinositol 4,5-bisphosphate, zebrafish, MDCK, kidney, oculocerebrorenal syndrome of Lowe
MeSH Terms
  • Adenosine Triphosphate/metabolism
  • Animals
  • Body Patterning
  • Calcium Signaling
  • Cell Line
  • Cilia/metabolism
  • Cilia/ultrastructure
  • Dogs
  • Epithelial Cells/cytology
  • Epithelial Cells/metabolism
  • Epithelial Cells/ultrastructure
  • Kidney Tubules, Proximal/cytology
  • Kidney Tubules, Proximal/ultrastructure*
  • Organogenesis
  • Phosphoric Monoester Hydrolases/genetics
  • Phosphoric Monoester Hydrolases/metabolism*
  • RNA, Small Interfering
  • Zebrafish/embryology
  • Zebrafish/metabolism
  • Zebrafish Proteins/genetics
  • Zebrafish Proteins/metabolism*
PubMed
22680056 Full text @ Traffic
Abstract

Lowe syndrome is an X-linked disorder characterized by cataracts at birth, mental retardation, and progressive renal malfunction that result from loss of function of the OCRL1 (oculocerebrorenal syndrome of Lowe) protein. OCRL1 is a lipid phosphatase that converts phosphatidylinositol 4,5-bisphosphate to phosphatidylinositol 4-phosphate. The renal pathogenesis of Lowe syndrome patients has been suggested to result from alterations in membrane trafficking, but this cannot fully explain the disease progression. We found that knockdown of OCRL1 in zebrafish caused developmental defects consistent with disruption of ciliary function, including body axis curvature, pericardial edema, hydrocephaly, and impaired renal clearance. In addition, cilia in the proximal tubule of the zebrafish pronephric kidney were longer in ocrl morphant embryos. We also found that knockdown of OCRL1 in polarized renal epithelial cells caused elongation of the primary cilium and disrupted formation of cysts in 3-dimensional cultures. Calcium release in response to ATP was blunted in OCRL1 knockdown cells, suggesting changes in signaling that could lead to altered cell function. Our results suggest a new role for OCRL1 in renal epithelial cell function that could contribute to the pathogenesis of Lowe syndrome.

Genes / Markers
Figures
Show all Figures
Expression
Phenotype
Mutations / Transgenics
Human Disease / Model
Sequence Targeting Reagents
Fish
Antibodies
Orthology
Engineered Foreign Genes
Mapping