Search Ontology:
ChEBI
vamorolone
- Term ID
- CHEBI:228304
- Synonyms
-
- (16alpha)-17,21-dihydroxy-16-methylpregna-1,4,9(11)-triene-3,20-dione
- 17,21-dihydroxy-16alpha-methylpregna-1,4,9(11)-triene-3,20-dione
- 17alpha,21-dihydroxy-16alpha-methylpregna-1,4,9(11)-triene-3,20-dione
- Agamree
- vamorolona
- vamorolone
- vamorolonum
- VBP 15
- VBP-15
- VBP15
- Definition
- A 3-oxo-Δ1,Δ4-steroid that is pregna-1,4,9(11)-trien-17-ol substituted by oxo, oxo, and hydroxy groups at positions 3, 20, and 21, respectively. It is approved by the FDA for the treatment of patients with Duchenne muscular dystrophy aged 2 years and older.
- References
-
- cas:13209-41-1
- drugbank:DB15114
- kegg.drug:D11000
- pmc:PMC9627259
- pubmed:23498916
- pubmed:23667681
- pubmed:24014378
- pubmed:25392236
- pubmed:27133900
- pubmed:28030841
- pubmed:29524454
- pubmed:29666400
- pubmed:29883261
- pubmed:30120816
- pubmed:30219580
- pubmed:30742306
- pubmed:30745312
- pubmed:31446438
- pubmed:31451516
- pubmed:32434278
- pubmed:32917814
- pubmed:32956407
- pubmed:35076703
- pubmed:36036925
- pubmed:36816559
- pubmed:37440999
- pubmed:37534133
- pubmed:37819629
- pubmed:37927274
- pubmed:38103149
- pubmed:38153112
- pubmed:38335499
- wikipedia.en:Vamorolone
- Ontology
- ChEBI ( EBI )
Phenotype
Phenotype resulting from vamorolone
Phenotype where environments contain vamorolone
Phenotype modified by environments containing vamorolone
Phenotype affecting vamorolone
Human Disease Model