PUBLICATION

Variant in EZR leads to defects in lens development

Authors
Zhou, N., He, M., Zhou, G., Fan, Q., Qi, Y.
ID
ZDB-PUB-240403-1
Date
2024
Source
Ophthalmic genetics   45(4): 363-371 (Journal)
Registered Authors
Keywords
Congenital cataract, ezrin, mutation, zebrafish
MeSH Terms
  • Animals
  • Lens, Crystalline*/metabolism
  • Lens, Crystalline*/pathology
  • Humans
  • Cytoskeletal Proteins*/genetics
  • Cataract*/genetics
  • Cataract*/pathology
  • Zebrafish*
  • Exome Sequencing
  • Pedigree*
  • Mutation, Missense*
  • Male
  • Female
  • Genetic Linkage
PubMed
38563525 Full text @ Ophthalmic Genet.
Abstract
Congenital cataract is a common cause of blindness. Genetic factors always play important role.
This study identified a novel missense variant (c.1412C>T (p.P471L)) in the EZR gene in a four-generation Chinese family with nuclear cataract by linkage analysis and whole-exome sequencing. A knockout study in zebrafish using transcription activator-like effector nucleases was carried out to gain insight into candidate gene function.
Conservative and functional prediction suggests that the P-to-L substitution may impair the function of the human ezrin protein. Histology showed developmental delays in the ezrin-mutated zebrafish, manifesting as multilayered lens epithelial cells. Immunohistochemistry revealed abnormal proliferation patterns in mutant fish.
The study suggests that ezrin may be involved in the enucleation and differentiation of lens epithelial cells.
Genes / Markers
Figures
Expression
Phenotype
Mutations / Transgenics
Human Disease / Model
Sequence Targeting Reagents
Fish
Antibodies
Orthology
Engineered Foreign Genes
Mapping