Zulian et al., 2014 - NIM811, a cyclophilin inhibitor without immunosuppressive activity, is beneficial in collagen VI congenital muscular dystrophy models. Human molecular genetics   23(20):5353-63 Full text @ Hum. Mol. Genet.
2 Genes / Markers
Marker Type Symbol Name
Gene col6a1 collagen, type VI, alpha 1
Gene dag1 dystroglycan 1