Ciapaite et al., 2019
- Pyridox(am)ine 5'-phosphate oxidase (PNPO) deficiency in zebrafish results in fatal seizures and metabolic aberrations.
Biochimica et biophysica acta. Molecular basis of disease
1866(3):165607
Full text @ BBA Molecular Basis of Disease
Target | Reagent |
---|---|
pnpo | CRISPR1-pnpo |
CRISPR2-pnpo |