van Karnebeek et al., 2019 - Bi-allelic GOT2 Mutations Cause a Treatable Malate-Aspartate Shuttle-Related Encephalopathy. American journal of human genetics   105(3):534-548 Full text @ Am. J. Hum. Genet.
Morpholino List (2 Records)
Target Reagent
got2a MO1-got2a
MO2-got2a