PUBLICATION

Development of thieno- and benzopyrimidinone inhibitors of the Hedgehog signaling pathway reveals PDE4-dependent and PDE4-independent mechanisms of action

Authors
Hempel, J.E., Cadar, A.G., Hong, C.C.
ID
ZDB-PUB-160316-4
Date
2016
Source
Bioorganic & medicinal chemistry letters   26(8): 1947-53 (Journal)
Registered Authors
Hong, Charles
Keywords
Eggmanone, Hedgehog signaling pathway, Phenotypic screening, Probe development, Suppressor of Fused
MeSH Terms
  • Cyclic Nucleotide Phosphodiesterases, Type 4/metabolism*
  • Dose-Response Relationship, Drug
  • HEK293 Cells
  • Hedgehog Proteins/antagonists & inhibitors*
  • Humans
  • Molecular Structure
  • Phosphodiesterase 4 Inhibitors/chemical synthesis
  • Phosphodiesterase 4 Inhibitors/chemistry
  • Phosphodiesterase 4 Inhibitors/pharmacology*
  • Pyrimidinones/chemical synthesis
  • Pyrimidinones/chemistry
  • Pyrimidinones/pharmacology*
  • Repressor Proteins/antagonists & inhibitors
  • Repressor Proteins/deficiency
  • Signal Transduction/drug effects*
  • Smoothened Receptor/antagonists & inhibitors
  • Structure-Activity Relationship
PubMed
26976215 Full text @ Bioorg. Med. Chem. Lett.
Abstract
From a high content in vivo screen for modulators of developmental patterning in embryonic zebrafish, we previously identified eggmanone (EGM1, 3) as a Hedgehog (Hh) signaling inhibitor functioning downstream of Smoothened. Phenotypic optimization studies for in vitro probe development utilizing a Gli transcription-linked stable luciferase reporter cell line identified EGM1 analogs with improved potency and aqueous solubility. Mechanistic profiling of optimized analogs indicated two distinct scaffold clusters: PDE4 inhibitors able to inhibit downstream of Sufu, and PDE4-independent Hh inhibitors functioning between Smo and Sufu. Each class represents valuable in vitro probes for elucidating the complex mechanisms of Hh regulation.
Genes / Markers
Figures
Expression
Phenotype
Mutations / Transgenics
Human Disease / Model
Sequence Targeting Reagents
Fish
Antibodies
Orthology
Engineered Foreign Genes
Mapping